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Patient Focused. Results Driven.



Transformative therapies for rare diseases with high unmet needs.


Innovative partnerships that create new opportunities in the rare disease field.


On our commitment to the patients, families, and communities we serve.


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Complete DiGeorge Anomaly

Children with complete DiGeorge Anomaly are born without a thymus gland, resulting in primary immunodeficiency. The disease is almost uniformly fatal within the first 24 months of life if untreated.


Farber Disease

Farber disease is an ultra-rare lysosomal storage disease caused by a mutation in both alleles of the ASAH1 gene, resulting in the deficiency of the lysosomal enzyme acid ceramidase.

February 21, 2019

Rachelle is a proven leader and operator with deep experience bringing valued medicines to market in complex, fast-moving business environments,

February 4, 2019

Abstracts highlighting the development of its investigational RVT-801 program and the natural history of Farber disease will be presented in Orlando, Florida, by Enzyvant and its collaborators at the 2019 WORLDSymposiumâ„¢

December 12, 2018

Enzyvant today announced the appointment of George O. Elston as Chief Financial Officer and Head of Corporate Development, further building the capabilities of the company.

Contact us for more information.